PrimeC has been given an ‘Orphan Drug’ status by the FDA (Food and Drug Administration) and EMA (European Medicines Agency).
| Avoid common pitfalls in EU orphan drug market access—learn how local expertise can help navigate pricing, reimbursement, ...
As we observe Rare Disease Day today, let us take a look at seven drugs poised to be approved to address rare diseases in ...
Porosome Therapeutics, Inc. (Porosome Therapeutics) today announced the Orphan Drug Designation of its cystic fibrosis therapy by the Food and Drug Administration (FDA). On February 10 ...
NICE publishes final draft guidance recommending efanesoctocog alfa as an option for treating and preventing bleeding in ...
TNG462 granted Orphan Drug Designation for treatment of pancreatic cancer –– Investigational New Drug (IND) application for TNG456, a ...
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Neurotech receives positive opinion for orphan status in Rett Syndrome from European drug regulatorNeurotech has received positive feedback from the European Medicines Agency (EMA) on its orphan drug application for NTI164 ...
February 28, 2025 (Investorideas.com Newswire) Investorideas.com, a global news source and expert investing resource, ...
The Food and Drug Administration (FDA) has granted Orphan Drug designation to EXG-34217 for the treatment of telomere biology disorders.
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