Initial interim 52-week results from Phase 2b Population Extension cohort of PRISM clinical trial to be presented by Dante Pieramici, M.D., a ...

A new mega-database of half a million mutations may flag new ways of treating genetic disease, scientists say.

Detailed price information for 4D Molecular Therapeutics Inc (FDMT-Q) from The Globe and Mail including charting and trades.

In this review of RNA therapies, we paint an overview of what’s going on in a field that is addressing a number of diseases.

Detailed price information for 4D Molecular Therapeutics Inc (FDMT-Q) from The Globe and Mail including charting and trades.

Genomic sequences visualization ... Children have different possible combination of genes. Vector illustration. gene cell therapy stock illustrations Cystic fibrosis genetics. Cystic fibrosis is an ...

Children whose cystic fibrosis is caused by a rare gene variant are excluded from a new treatment which could potentially slow the decline in their lung function, it has emerged. A group of ...

Viral and nonviral clinical trials have established proof-of-principle for gene transfer into the cystic fibrosis (CF) lung. It is currently unknown whether gene transfer efficiency is sufficient ...

The research is published in the journal Nature. The study comprehensively analyzed "cis-regulatory elements" (CREs), which are the DNA sequences that regulate gene transcription. This work sheds ...

for the treatment of cystic fibrosis in patients with at least one F508del mutation or another treatment-responsive mutation in the CFTR gene. The fixed-dose triple-combination therapy ...