In a report released yesterday, Tazeen Ahmad from Bank of America Securities maintained a Buy rating on Ultragenyx Pharmaceutical (RARE – ...

On a recent visit to Washington DC, Ho sat down with GEN Editorial Director Kevin Davies, PhD, to discuss Denali’s progress ...

Ultragenyx Pharmaceutical RARE announced that the European Commission (EC) has expanded the eligible patient population for ...

Data from the first patients enrolled into Regenxbio's trial of its gene therapy for rare inherited disease mucopolysaccharidosis type I (MPS I) – also known as Hurler syndrome – has shown the ...

In the largest study of its kind globally, UK clinicians and researchers at Royal Manchester Children’s Hospital (RMCH) part of Manchester University NHS Foundation Trust (MFT), and Great Ormond ...

Fast-growing wildfires raging in Los Angeles killed at least two people on Wednesday, destroying hundreds of buildings, scorching hillsides and prompting officials to order some 70,000 people to ...

A state of emergency has been declared in Russia's western city of Engels, according to the region's governor. It comes after Ukraine said it was behind a drone strike on a Russian oil base in the ...

DHAKA: Ailing former Bangladesh PM and BNP chief Khaleda Zia on Wednesday met her son Tarique Rahman in London after more than seven years, a reunion made possible by a changed political scenario ...

A force fighting Sudan’s army in a brutal civil war committed massacres and rape that amount to genocide, the Secretary of State said, two decades after a finding of genocide in the same region ...

Chinese state media said at least 126 people had died in the magnitude 7.1 quake near an area of religious significance in Tibet. It was felt in neighboring Nepal. By David PiersonBerry Wang and ...

“Toxicant-induced loss of tolerance” may be an underlying cause of the wide range of symptoms experienced by residents of East Palestine. Use SecureDrop, an anonymity tool for journalists and ...

The Facebook-parent also elected Charlie Songhurst, an investor and former Microsoft executive, as well as John Elkann, CEO of Exor, a holding company controlled by Italy’s Agnelli family with ...