(AskBio), a gene therapy company wholly owned and independently operated as a subsidiary of Bayer AG, today announced that AB ...

The firm says both the company’s Pompe and Fabry disease franchises have “significant levers that could be used to generate a steady stream of revenue growth.” It is a buyer on the stock into 2025.

Amicus Therapeutics Inc (FOLD) reports a 37% revenue increase and raises full-year guidance, despite ongoing litigation challenges.

11.3. The Advisory Committee recommended that avalglucosidase alfa for the treatment of late onset Pompe disease be funded with a medium priority.

The Delhi High Court has directed the Union Government to establish the National Fund for Rare Diseases (NFRD). What are rare diseases? What are the government policies for rare diseases? Take a look.

Group 3 covers conditions like Gaucher Disease and Pompe Disease, where treatment is available but complicated by high costs ...

Cardiovascular disease is a group of conditions that affect your heart and blood vessels. It's sometimes also called heart disease. Conditions that affect your heart and blood vessels can include ...

Motivated patients with rare diseases are using social media widely, making it an effective way to reach patients for trial ...

He added that registries from specific companies can be useful resources, referencing Sanofi’s Rare Disease Registries which records information about rare conditions such as Gaucher disease, Fabry ...

Lady Gaga debuted her new single “Disease” — an electro-pop song about curing a lover’s “tortured” disease — on Thursday night. The upbeat track was written by Michael Polansky ...

The Mother Monster is back. Marking her return to the peak pop form that put her on the map, Lady Gaga has shared a new song, “Disease,” the first single from her forthcoming album. Stream it below.